Genetic disease

Source: McGill University Health Centre Summary: An international team’s work has shed new light on a molecule called TIM-3 that might play a key role in the regulation of the immune response. Following the 2018 Nobel Prize for Medicine, global attention is now more than ever turned toward the promise of immunotherapyRead More →

Gene therapy to treat a rare inherited vision loss

Source: Spark Therapeutics Summary: The US-FDA approved a novel gene therapy – Luxturna, first of its kind to treat children and adult patients with a rare inherited form of vision loss that may result in blindness. Spark Therapeutics at Philadelphia is a fully integrated late clinical-stage gene therapy company. Its investigational therapiesRead More →